Mini-PCDH15 gene therapy rescues hearing in a mouse model of Usher syndrome type 1F

Proposed therapy, developed in a Pcdh15-deficient mouse, for progressive loss of vision in human Usher syndrome

WO2020219990A1 - Aav vectors encoding mini-pcdh15 and uses thereof - Google Patents

Mini-PCDH15 gene therapy rescues hearing in a mouse model of Usher syndrome type 1F

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PDF) Proposed therapy, developed in a Pcdh15-deficient mouse, for progressive loss of vision in human Usher Syndrome

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Mini-PCDH15 gene therapy rescues hearing in a mouse model of Usher syndrome type 1F

Dual AAV-based PCDH15 gene therapy achieves sustained rescue of visual function in a mouse model of Usher syndrome 1F - ScienceDirect